Research for new therapies for Pompe disease is still a little uncertain for the immediate future, but clinical trials for Gene Therapy have begun to reopen after the programmes were paused earlier this year due to Covid-19.
We have updated the table of clinical trials (below) with the latest information provided to us, but please be aware that the situation may change as winter approaches and a second wave of Covid-19 puts NHS hospitals under strain once again.
UK Study Centres
The spreadsheet contains links to the studies on the NIH register of clinical trials, ClinicalTrials.gov and the status of studies in the UK. We will update the spreadsheet as new studies are introduced and as more information becomes available.
If you are interested in joining one of the studies, you should first discuss it with your consultant at the Highly Specialised LSD Centre you attend. You should be able to transfer to another centre if yours is not offering the trial you would like to join.
If you can’t open the spreadsheet, please contact the Pompe Support Network at firstname.lastname@example.org.
To check centres in other regions you can click on the links in our spreadsheet or search through these international registries of clinical studies:
NIH Clinical Trials.gov
EMA European Clinical Trials Register
WHO International Clinical Trials Register